Intellectual disability-eye abnormalities-microcephaly-peripheral spasticity syndrome Advocacy Hub | UniteRare

Regulatory Watchboard

2 events

Nov 2025Gene Replacement Therapy for Treatment of Paediatric Patients With CTNNB1 Neurodevelopmental Syndrome

CTNNB1 Foundation — PHASE1, PHASE2

TrialRECRUITING

Jun 2024CTNNB1 Neurodevelopmental Syndrome - Natural History Study

University Medical Centre Ljubljana

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

Total programs

No financial assistance programs currently listed for Intellectual disability-eye abnormalities-microcephaly-peripheral spasticity syndrome.
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Clinical Trial Landscape

No active clinical trials currently recruiting for Intellectual disability-eye abnormalities-microcephaly-peripheral spasticity syndrome.
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