Immune-mediated thrombotic thrombocytopenic purpura

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At a Glance

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Regulatory Watchboard

4 events
Nov 2025An Open-label Study of Intravenous Immunoglobulin (5%) for the Treatment of Primary Immune Thrombocytopenia

Grand Shuyang Life Sciences (Chengdu) Co., Ltd. — PHASE3

TrialRECRUITING
May 2025A Pilot Study of Efgartigimod for Immune-mediated Thrombotic Thrombocytopenic Purpura (iTTP)

University of Minnesota — PHASE2

TrialRECRUITING
Oct 2022Improvement of Immunologic and Molecular Techniques for the Diagnosis and Follow-up of Patients With Thrombotic Thrombocytopenic Purpura

Fundación Española de Hematología y Hemoterapía

TrialACTIVE NOT RECRUITING
Mar 2021Retrospective Analysis of the Efficiency of Caplacizumab in the Treatment of aTTP

University of Cologne

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

2 programs

FINANCIAL LANDSCAPE SUMMARY

2

Total programs

2

Open now

1

Copay cards

Copay Assistance1

Doptelet

Sobi, Inc.

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Patient Assistance Programs1

Adzynma

TAKEDA PHARMACEUTICALS AMERICA, INC.

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Approved Treatments

3 FDA-approved

Doptelet

(avatrombopag)Orphan drug

Sobi, Inc.

12.1 Mechanism of Action Avatrombopag is an orally bioavailable, small molecule TPO receptor agonist that stimulates proliferation and differentiation...

Approved Jul 2025FDA label ↗

Adzynma

(APADAMTASE ALFA)Orphan drug

TAKEDA PHARMACEUTICALS AMERICA, INC.

12.1 Mechanism of Action ADZYNMA is a recombinant form of the endogenous ADAMTS13. ADAMTS13 is a plasma zinc metalloprotease that regulates the activi...

Approved Nov 2023FDA label ↗

Cablivi

(CAPLACIZUMAB)Orphan drugstandard

Genzyme Corporation

12.1 Mechanism of Action Caplacizumab-yhdp targets the A1-domain of vWF, and inhibits the interaction between vWF and platelets, thereby reducing both...

FDA label ↗

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Clinical Trial Landscape

3 active trials
1Phase 2
2Unknown
3Total recruiting
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Recent News & Research

No recent news articles indexed yet for Immune-mediated thrombotic thrombocytopenic purpura.
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Specialist Network

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