Hypophosphatasia Advocacy Hub | UniteRare

At a Glance

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Regulatory Watchboard

6 events

Sep 2025A Study to Assess Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of ALE1 in Healthy Adults and Adults With Hypophosphatasia in Order to Identify Suitable Doses of ALE1

Alesta Therapeutics — PHASE1, PHASE2

TrialRECRUITING

May 2024Phase 3 Study of ALXN1850 in Treatment-Naïve Pediatric Participants With HPP

Alexion Pharmaceuticals, Inc. — PHASE3

TrialACTIVE NOT RECRUITING

Apr 2024Phase 3 Study of ALXN1850 in Pediatric Participants With HPP Previously Treated With Asfotase Alfa

Alexion Pharmaceuticals, Inc. — PHASE3

TrialACTIVE NOT RECRUITING

Aug 2022A Prospective Sub-Study of the Global Hypophosphatasia Registry

Alexion Pharmaceuticals, Inc.

TrialRECRUITING

Aug 2021United States Hypophosphatasia Molecular Research Center

Children's Mercy Hospital Kansas City

TrialRECRUITING

Jan 2015Registry of Patients With Hypophosphatasia

Alexion Pharmaceuticals, Inc.

TrialENROLLING BY INVITATION

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

Total programs

No financial assistance programs currently listed for Hypophosphatasia.
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Clinical Trial Landscape

6 active trials

2Phase 3

3Unknown

1PHASE1, PHASE2

6Total recruiting

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Recent News & Research

No recent news articles indexed yet for Hypophosphatasia.
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Specialist Network

Top 6 by expertise

Keiichi Ozono

Osaka University Hospital

Score 341 trial38 pubs

Priya Kishnani, MD

Duke University

📍 DURHAM, NC

Score 139 trials

Richard Eastell, MD FRCP

University of Sheffield

Score 131 trial

Eric Rush

Children's Mercy Hospital Kansas City

Score 121 trial13 pubs

Richard Eastell

University of Sheffield

Score 41 trial3 pubs

Valentin S. Schäfer, Univ.-Prof. Dr. med. MUDr.

University Hospital of Bonn

Score 31 trial

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