Advocacy intelligence hub — real-time data for patient organizations
QED Therapeutics, a BridgeBio company — PHASE2
BioMarin Pharmaceutical — PHASE2
BioMarin Pharmaceutical — PHASE3
QED Therapeutics, a BridgeBio company — PHASE2, PHASE3
BioMarin Pharmaceutical — PHASE3
QED Therapeutics, a BridgeBio company
BioMarin Pharmaceutical
Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
FINANCIAL LANDSCAPE SUMMARY
Total programs
Andrew Dauber, MS MMSc, M.D
Children's National Research Institute
📍 CINCINNATI, OH
Genevieve Baujat
Hopital Necker
Robert Olney, MD, MD
Nemours Children's Clinic
📍 JACKSONVILLE, FL
Michael Bober, MD, PhD, MD
Alfred I. duPont Hospital for Children
📍 WILMINGTON, DE