Advocacy intelligence hub — real-time data for patient organizations
Thiola: FDA approved
THIOLA EC is indicated, in combination with high fluid intake, alkali, and diet modification, for the prevention of cystine stone formation in adults and pediatric patients 20 kg and greater with severe homozygous cystinuria, who are not responsive to these measures alone.
Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
FINANCIAL LANDSCAPE SUMMARY
Total programs
Open now
Copay cards
Copay Assistance1
Betaine Anhydrous
Eton Pharmaceuticals, Inc.
Cystadane
(BETAINE)Orphan drugstandardRecordati Rare Diseases
Methylating Agent [EPC]
Betaine Anhydrous
(BETAINE ANHYDROUS)Orphan drugstandardEton Pharmaceuticals, Inc.
Methylating Agent [EPC]
Browse all Homocystinuria due to cystathionine beta-synthase deficiency news →
View all Homocystinuria due to cystathionine beta-synthase deficiency specialists →