Hemophilia A

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At a Glance

Live from database

Regulatory Watchboard

10 events
Apr 2026Nuwiq Dosing and Outcomes In the ManagEment of Women/Girls With Haemophilia A Needing FVIII Treatment for Surgery

Octapharma — PHASE4

TrialRECRUITING
Mar 2026A Gene Therapy Study of SPK-8011QQ in Adults With Severe or Moderately Severe Hemophilia A

Hoffmann-La Roche — PHASE1, PHASE2

TrialNOT YET RECRUITING
Mar 2026Liver Biopsy Following Gene Therapy For Hemophilia

St. Jude Children's Research Hospital

TrialNOT YET RECRUITING
Nov 2025A Research Study Looking at How Food Intake Affects Inno8 in the Body of Healthy People

Novo Nordisk A/S — PHASE1

TrialRECRUITING
Nov 2025Factor VIII Inhibitor Bypass Activity (FEIBA) Versus Fresh Frozen Plasma As First Line Therapy For Bleeding After Cardiac Surgery

Northwell Health — PHASE2

TrialRECRUITING
Oct 2025A Study to Learn About the Study Medicine -Hympavzi in Congenital Hemophilia Patients Without Inhibitors in Japan.

Pfizer

TrialACTIVE NOT RECRUITING
Oct 2025A Research Study Looking at How Different Doses of Study Medicine (Inno8) Work in the Body of People With Haemophilia A

Novo Nordisk A/S — PHASE1

TrialRECRUITING
May 2025Post-marketing Surveillance (Special Use-results Surveillance) on Treatment With Alhemo

Novo Nordisk A/S

TrialENROLLING BY INVITATION
Mar 2025Assessing Different FVIII Doses and Frequencies in Immune Tolerance Induction (ITI) with ADVATE Among Hemophilia a Boys with Inhibitor (INITIATE Study)

Runhui WU — PHASE4

TrialRECRUITING
Feb 2025Pharmacokinetic Comparison of Efanesoctocog Alfa vs Other EHL-rFVIII Products in Participants With Severe Haemophilia A

Swedish Orphan Biovitrum — PHASE1

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

3 programs

FINANCIAL LANDSCAPE SUMMARY

3

Total programs

3

Open now

3

Copay cards

Copay Assistance3

ROCTAVIAN

BioMarin

OpenContact for detailsApply ↗

ALTUVIIIO

Sanofi

OpenContact for detailsApply ↗

Hemlibra

Genentech

OpenContact for detailsApply ↗

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Approved Treatments

7 FDA-approved

ALTUVIIIO

(ANTIHEMOPHILIC FACTOR (RECOMBINANT), FC-VWF-XTEN FUSION PROTEIN-EHTL)Orphan drug

Bioverativ Therapeutics Inc.

FDA label ↗

ROCTAVIAN

(VALOCTOCOGENE ROXAPARVOVEC-RVOX)Orphan drug

BioMarin Pharmaceutical Inc.

FDA label ↗

Hemlibra

(EMICIZUMAB)Orphan drug

Genentech, Inc.

FDA label ↗

Alhemo

(CONCIZUMAB)Orphan drugstandard

Novo Nordisk

FDA label ↗

HYMPAVZI

(MARSTACIMAB-HNCQ)Orphan drug

Pfizer Laboratories Div Pfizer Inc

FDA label ↗

Humate-P

(Antihemophilic factor/von Willebrand factor complex (human), dried, pasteurized)Orphan drugstandard

CSL Behring

Qfitlia

(FITUSIRAN)Orphan drugstandard

Genzyme Corporation

FDA label ↗

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Clinical Trial Landscape

19 active trials
4Phase 3
4Phase 4
1Phase 1
1N/A
6Unknown
1PHASE1, PHASE2
2EARLY_PHASE1
19Total recruiting
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Recent News & Research

6 articles
HamostaseologieApr 21, 2026

Perioperative Management for Port Catheter Procedures in Pediatric Patients with Severe Hemophilia and Inhibitors.

The objective of this systematic study was to assess the perioperative management and outcome of surgery in pediatric patients with hemophilia A/B and inhibitors compared to nonhemophilic pediatric pa...

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Journal of investigational allergology & clinical immunologyApr 21, 2026

Acquired Hemophilia A Following Omalizumab Treatment in a Patient With Chronic Spontaneous Urticaria.

Acquired Hemophilia A Following Omalizumab Treatment in a Patient With Chronic Spontaneous Urticaria.

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Archives of medical researchApr 17, 2026

Factor VIII Pharmacokinetics in Mexican Patients with Hemophilia A.

Treatment of patients with severe hemophilia A requires the replacement of deficient factor VIII. To reach the international standards of care, an optimal dose of factor VIII should be administered ba...

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La Revue du praticienMar 31, 2026

[Acquired hemophilia A].

[Acquired hemophilia A].

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BioDrugs : clinical immunotherapeutics, biopharmaceuticals and gene therapyMar 25, 2026

Immunogenicity of Gene and Cell Therapies.

Gene and cell therapies have been gaining popularity with market approvals by the US Food and Drug Administration, European Medicines Agency, and other regulatory bodies. Adeno-associated viral vector...

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Expert review of clinical pharmacologyMar 16, 2026

Factor-VIII mimetic bispecific antibodies for the treatment of hemophilia A: an update.

Bispecific antibodies are used to treat various conditions, with notable results in hemophilia A, a rare bleeding disorder characterized by reduced or absent activity of the coagulation factor VIII (F...

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Specialist Network

Top 6 by expertise

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