GM1 gangliosidosis type 1

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At a Glance

Live from database

Regulatory Watchboard

1 event
Mar 2021First-in-Human Study of TSHA-101 Gene Therapy for Treatment of Infantile Onset GM2 Gangliosidosis

Dr. Anupam Sehgal — PHASE1

TrialACTIVE NOT RECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

0

Total programs

No financial assistance programs currently listed for GM1 gangliosidosis type 1.
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Clinical Trial Landscape

No active clinical trials currently recruiting for GM1 gangliosidosis type 1.
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Recent News & Research

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Specialist Network

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