Gaucher disease type 3

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At a Glance

Live from database

Regulatory Watchboard

6 events
Mar 2025High-Dose Ambroxol in Pediatric Type III Gaucher Disease (GD3)

Agyany Pharma LTD — NA

TrialACTIVE NOT RECRUITING
Apr 2024Effect of Enzyme Replacement Therapy on Cardiac Function in Children With Gaucher Disease Type 3

Noha Osman — NA

TrialENROLLING BY INVITATION
Nov 2023A Study of the Safety and Preliminary Efficacy of LY-M001 Injection in the Treatment of Adult Patients with Gaucher Disease Type I

He Huang — NA

TrialRECRUITING
Jan 2023MAGNETIC RESONANCE SPECTROSCOPY BIOMARKERS IN TYPE 3 GAUCHER DISEASE (GD3)

University of Minnesota — NA

TrialRECRUITING
Apr 2022Study to Evaluate the Efficacy and Safety of Venglustat in Adult and Pediatric Patients With Gaucher Disease Type 3

Sanofi — PHASE3

TrialACTIVE NOT RECRUITING
Jan 2014Gaucherite - A Study to Stratify Gaucher Disease

Cambridge University Hospitals NHS Foundation Trust — NA

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

0

Total programs

No financial assistance programs currently listed for Gaucher disease type 3.
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Clinical Trial Landscape

6 active trials
1Phase 3
5N/A
6Total recruiting
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Recent News & Research

No recent news articles indexed yet for Gaucher disease type 3.
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Specialist Network

Top 6 by expertise

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