Advocacy intelligence hub — real-time data for patient organizations
Healing Hope International
Azevan Pharmaceuticals — PHASE2
Spinogenix — PHASE2, PHASE3
Hospices Civils de Lyon
Mirum Pharmaceuticals, Inc. — PHASE2
Université de Sherbrooke — PHASE2
University of North Carolina, Chapel Hill — NA
Holland Bloorview Kids Rehabilitation Hospital — PHASE2
Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
FINANCIAL LANDSCAPE SUMMARY
Total programs
Elizabeth Smith, PhD
Cincinnati Children's Hospital
📍 Cincinnati, Ohio
Anne Wheeler, PhD
RTI International
📍 Research Triangle Park, North Carolina
Forbes D Porter, M.D.
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
📍 Bethesda, Maryland
Maithé TAUBER, MD
University Hospital, Toulouse
Randi J Hagerman, MD, M.D
M.I.N.D. Institute at University of California at Davis, Sacramento CA
📍 DAVIS, CA
Paul Wang, M.D.
Seaside Therapeutics, Inc.