Familial lipoprotein lipase deficiency Advocacy Hub | UniteRare

At a Glance

Live from database

🔬

Regulatory Watchboard

5 events

Jan 2026CS-121 APOC3 Base Editing in Children and Adolescents With Hyperchylomicronemia

Shanghai Jiao Tong University School of Medicine — EARLY_PHASE1

TrialRECRUITING

Oct 2025CS-121 APOC3 Base Editing in FCS

CorrectSequence Therapeutics Co., Ltd — EARLY_PHASE1

TrialRECRUITING

Feb 2022A Study of Olezarsen (Formerly Known as AKCEA-APOCIII-LRX) Administered to Adults With Familial Chylomicronemia Syndrome (FCS) Previously Treated With Volanesorsen

Ionis Pharmaceuticals, Inc. — PHASE3

TrialACTIVE NOT RECRUITING

Nov 2021A Study of Olezarsen (Formerly Known as AKCEA-APOCIII-LRx) in Participants With Familial Chylomicronemia Syndrome (FCS)

Ionis Pharmaceuticals, Inc. — PHASE3

TrialACTIVE NOT RECRUITING

Dec 2019Postprandial Fatty Acid Metabolism in Subjects With Lipoprotein Lipase Deficiency

Université de Sherbrooke — NA

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

1 program

FINANCIAL LANDSCAPE SUMMARY

Total programs

Open now

Copay cards

Copay Assistance1

REDEMPLO

Unknown

OpenContact for detailsApply ↗

View all support programs on disease page →

Clinical Trial Landscape

5 active trials

2Phase 3

1N/A

2EARLY_PHASE1

5Total recruiting

Search clinical trials for Familial lipoprotein lipase deficiency →

Recent News & Research

No recent news articles indexed yet for Familial lipoprotein lipase deficiency.
Search PubMed for Familial lipoprotein lipase deficiency →

Browse all Familial lipoprotein lipase deficiency news →

Specialist Network

Top 5 by expertise

Philippe Moulin, MD

Hospices Civils de Lyon

Score 161 trial

YALIANG LI

CorrectSequence Therapeutics (Shanghai) Co., Ltd

Score 112 trials1783 pubs

Daniel Gaudet, MD, Ph.D.

ECOGENE-21 Clinical Trial Center / Centre de santé et de services sociaux de Chicoutimi, Chicoutimi Hospital, Quebec, Canada

Score 41 trial

André Carpentier

Université de Sherbrooke

Score 32 trials20 pubs

Robert Eckel, MD, MD

University of Colorado, Denver

📍 AURORA, CO

Score 21 trial

View all Familial lipoprotein lipase deficiency specialists →

Quick Actions

📄

View Disease Page

Full profile, treatments, community

🔬

Search Clinical Trials

Find recruiting studies now

🩺

Find Specialists

Ranked by expertise & trials

💰

Financial Assistance

Copay cards, PAPs, grants

📰