Familial chylomicronemia syndrome

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At a Glance

Live from database

Regulatory Watchboard

2 events
Dec 2024

Tryngolza: FDA approved

adjunct to diet to reduce triglycerides in adults with familial chylomicronemia syndrome (FCS)

FDAcompleted
Sep 2024Study of RN0361in Adult Healthy Subjects and Adult Hypertriglyceridemic Subjects

Ikaria Bioscience Pty Ltd — PHASE1, PHASE2

TrialACTIVE NOT RECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

2 programs

FINANCIAL LANDSCAPE SUMMARY

2

Total programs

2

Open now

1

Copay cards

Copay Assistance1

Redemplo

Arrowhead Pharmaceuticals, Inc.

OpenContact for details

Patient Assistance Programs1

Tryngolza

Ionis Pharmaceuticals

OpenContact for details

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Approved Treatments

2 FDA-approved

Redemplo

(plozasiran)Orphan drug

Arrowhead Pharmaceuticals, Inc.

Approved Nov 2025FDA label ↗

Tryngolza

(olezarsen)Orphan drug

Ionis Pharmaceuticals

12.1 Mechanism of Action Olezarsen is an ASO-GalNAc 3 conjugate that binds to apoC-III mRNA leading to mRNA degradation and resulting in a reduction o...

Approved Dec 2024FDA label ↗

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Clinical Trial Landscape

1 active trial
1PHASE1, PHASE2
1Total recruiting
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Recent News & Research

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Specialist Network

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