Essential thrombocythemia

Advocacy intelligence hub — real-time data for patient organizations

View full disease page →Search clinical trials →
Download CSV

At a Glance

Live from database

Regulatory Watchboard

10 events
Jun 2026WELL-MPN: A Digital Lifestyle App for Patients With MPNs

Brigham and Women's Hospital — NA

TrialNOT YET RECRUITING
May 2026Study of Pelabresib add-on to Ruxolitinib in Japanese Adult Patients With Myelofibrosis

Novartis Pharmaceuticals — PHASE1

TrialNOT YET RECRUITING
May 2026Selinexor and Pacritinib in JAK Inhibitor-naïve MF Patients With Cytopenias

John Mascarenhas — PHASE2

TrialNOT YET RECRUITING
Apr 2026A Phase 3 Study of Pelabresib (DAK539) and Ruxolitinib in Myelofibrosis (MF)

Novartis Pharmaceuticals — PHASE3

TrialNOT YET RECRUITING
Apr 2026A Phase 1 Study of PRT12396 in Participants With Select Myeloproliferative Neoplasms

Prelude Therapeutics — PHASE1

TrialRECRUITING
Feb 2026Registry Platform Myelofibrosis and Anemia

iOMEDICO AG

TrialRECRUITING
Dec 2025A ELN-Multicenter Study on Phenotypic Evolution and Clinical Outcomes

FROM- Fondazione per la Ricerca Ospedale di Bergamo- ETS

TrialRECRUITING
Oct 2025A Study to Evaluate INCA035784 in Participants With Myeloproliferative Neoplasms

Incyte Corporation — PHASE1

TrialRECRUITING
Jun 2025A Phase 1 Study to Assess STP938 as a Monotherapy in Adults With High Risk Essential Thrombocythaemia

Step Pharma, SAS — PHASE1

TrialRECRUITING
Feb 2025Study of Momelotinib in Combination With Luspatercept in Participants With Transfusion Dependent Myelofibrosis

GlaxoSmithKline — PHASE2

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

7 programs

FINANCIAL LANDSCAPE SUMMARY

7

Total programs

6

Open now

3

Copay cards

4

Travel grants

Copay Assistance3

FERRIPROX

Chiesi reinforcement _Self-correction:_ The user asked for the primary manufacturer/company that owns the rights. Chiesi is the entity. Final string: Chiesi

OpenContact for detailsApply ↗

Agrylin

Takeda

OpenContact for detailsApply ↗

Anagrelide

Takeda

OpenContact for detailsApply ↗

Travel Grants4

CancerCare Co-pay Assistance for Myeloproliferative Neoplasms

CancerCare

OpenContact for detailsApply ↗

Ferriprox Patient Enrollment (Chiesi USA)

Contact for detailsApply ↗

Takeda Here2Assist Program

Takeda Oncology

OpenContact for detailsApply ↗

Takeda Oncology Co-Pay Assistance Progam

Takeda Oncology

OpenContact for detailsApply ↗

View all support programs on disease page →

Approved Treatments

1 FDA-approved

Agrylin

(Anagrelide)Orphan drug

Takeda Development Center Americas, Inc.

12.1 Mechanism of Action The precise mechanism by which anagrelide reduces blood platelet count is unknown. In cell culture studies, anagrelide suppre...

Approved Mar 1997FDA label ↗

View full treatment details on disease page →

Clinical Trial Landscape

38 active trials
6Phase 3
13Phase 2
3Phase 1
3N/A
8Unknown
5PHASE1, PHASE2
38Total recruiting
Search clinical trials for Essential thrombocythemia

Recent News & Research

No recent news articles indexed yet for Essential thrombocythemia.
Search PubMed for Essential thrombocythemia

Browse all Essential thrombocythemia news →

Specialist Network

Top 6 by expertise

View all Essential thrombocythemia specialists →

Quick Actions