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FINANCIAL LANDSCAPE SUMMARY
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Kuvan
BioMarin Pharmaceutical, Inc.
Kuvan
(sapropterin)Orphan drugstandardBioMarin Pharmaceutical, Inc.
12.1 Mechanism of Action KUVAN is a synthetic form of BH4, the cofactor for the enzyme phenylalanine hydroxylase (PAH). PAH hydroxylates Phe through a...
Janaina Dovidio
Isabela F Lopes
Laís C Silva
Marta Ribeiro
Centro Hospitalar Universitário de Lisboa Central.
Mafalda Rebelo
Centro Hospitalar Universitário de Lisboa Central.
Charles Marques Lourenço
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