Dentatorubral pallidoluysian atrophy Advocacy Hub | UniteRare

At a Glance

Live from database

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4Recruiting trials

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1Specialists

Regulatory Watchboard

5 events

Nov 2025Personalized Antisense Oligonucleotide for A Single Participant (nL62541) With ATN1 Gene Mutation

n-Lorem Foundation — PHASE1, PHASE2

TrialNOT YET RECRUITING

Oct 2024Personalized Antisense Oligonucleotide for A Single Participant With ATN1 Gene Mutation

n-Lorem Foundation — PHASE1, PHASE2

TrialACTIVE NOT RECRUITING

Feb 2024Personalized Antisense Oligonucleotide Therapy for a Single Participant with ATN1 Gene Mutation

n-Lorem Foundation — PHASE1, PHASE2

TrialACTIVE NOT RECRUITING

May 2022Dentatorubral-pallidoluysian Atrophy Natural History and Biomarkers Study

University College, London

TrialRECRUITING

Mar 2021CureDRPLA Global Patient Registry

CureDRPLA

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

Total programs

No financial assistance programs currently listed for Dentatorubral pallidoluysian atrophy.
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Clinical Trial Landscape

4 active trials

2Unknown

2PHASE1, PHASE2

4Total recruiting

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Recent News & Research

No recent news articles indexed yet for Dentatorubral pallidoluysian atrophy.
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Specialist Network

Top 1 by expertise

Paola Giunti

University College, London

Score 41 trial4 pubs

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