Danon disease

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At a Glance

Live from database

Regulatory Watchboard

3 events
Dec 2023Danon Disease Natural History Study

Rocket Pharmaceuticals Inc.

TrialRECRUITING
Sep 2023A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease

Rocket Pharmaceuticals Inc. — PHASE2

TrialRECRUITING
Jan 2010Precision Diagnosis and Risk Stratification of Rare Cardiomyopathies Based on Novel Cardiac Magnetic Resonance Techniques

Chinese Academy of Medical Sciences, Fuwai Hospital — NA

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

0

Total programs

No financial assistance programs currently listed for Danon disease.
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Clinical Trial Landscape

3 active trials
1Phase 2
1N/A
1Unknown
3Total recruiting
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Recent News & Research

No recent news articles indexed yet for Danon disease.
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Specialist Network

Top 6 by expertise

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