Cystinosis

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At a Glance

Live from database

Regulatory Watchboard

10 events
Apr 2026Non-invasive Characterisation of Oral Carcinomas in Patients With Fanconi Anaemia

Institut Jean-Godinot — NA

TrialNOT YET RECRUITING
Jan 2026Cystinosis and Mitochondrial Metabolism

Hospices Civils de Lyon — NA

TrialNOT YET RECRUITING
Oct 2023PK and PD Study of NPI-001 and Cysteamine Bitartrate

Nacuity Pharmaceuticals, Inc. — PHASE1, PHASE2

TrialRECRUITING
Jan 2023Early Trial of Allogeneic Hematopoietic Stem Cell Transplantation for Patients Who Will Receive a Kidney Transplant From the Same Donor

Alice Bertaina — PHASE1, PHASE2

TrialRECRUITING
Nov 2022A Long-Term Follow-Up Study of Participants With Cystinosis Who Previously Received CTNS-RD-04

Stephanie Cherqui — NA

TrialENROLLING BY INVITATION
May 2022Development of Health-related Quality of Life Instrument for Patients With Cystinosis

Cystinose Stiftung — NA

TrialRECRUITING
Mar 2022Genetic Newborn Screening for Cystinosis and Primary Hyperoxaluria

Cystinose Stiftung — NA

TrialRECRUITING
Jul 2020Observational Study to Assess the Quality of Life in Nephropathic Cystinosis Patients

Chiesi SA/NV

TrialENROLLING BY INVITATION
Apr 2017European Cystinosis Cohort

Institut National de la Santé Et de la Recherche Médicale, France

TrialRECRUITING
Jan 1979Use of Cysteamine in the Treatment of Cystinosis

National Human Genome Research Institute (NHGRI) — NA

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

3 programs

FINANCIAL LANDSCAPE SUMMARY

3

Total programs

3

Open now

3

Copay cards

Copay Assistance3

Thiola EC

Travere

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MESNA

Baxter

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PROCYSBI

Amgen

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Clinical Trial Landscape

8 active trials
4N/A
2Unknown
2PHASE1, PHASE2
8Total recruiting
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Recent News & Research

No recent news articles indexed yet for Cystinosis.
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Specialist Network

Top 6 by expertise

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