Advocacy intelligence hub — real-time data for patient organizations
Institut Jean-Godinot — NA
Nacuity Pharmaceuticals, Inc. — PHASE1, PHASE2
Alice Bertaina — PHASE1, PHASE2
Stephanie Cherqui — NA
Cystinose Stiftung — NA
Cystinose Stiftung — NA
Chiesi SA/NV
Institut National de la Santé Et de la Recherche Médicale, France
National Human Genome Research Institute (NHGRI) — NA
Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
FINANCIAL LANDSCAPE SUMMARY
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Stephanie Cherqui, PhD
University of California San Diego
📍 La Jolla, California
William A Gahl, M.D.
National Human Genome Research Institute (NHGRI)
📍 Bethesda, Maryland
Julia Hannah Quitmann, PD Dr.
Department of Medical Psychology, University Medical Center Hamburg-Eppendorf, Hamburg, Germany
📍 Hamburg
Ranjan Dohil, M.D
University of California, San Diego
📍 SAN DIEGO, CA
Dieter Haffner
Liver and Metabolic Diseases
Galina V Nesterova, MD
National Human Genome Research Institute (NHGRI)
📍 BALTIMORE, MD