Cushing disease

Advocacy intelligence hub — real-time data for patient organizations

View full disease page →Search clinical trials →
Download CSV

At a Glance

Live from database

Regulatory Watchboard

10 events
Apr 2026FET PET/CT Imaging To Localize Pituitary Adenomas In Cushing Disease

Mayo Clinic — EARLY_PHASE1

TrialNOT YET RECRUITING
Mar 2026DDAVP for Pituitary Adenoma

National Institute of Neurological Disorders and Stroke (NINDS) — NA

TrialRECRUITING
Oct 2025Use of [18F]FET PET-MRI to Improve Detection of Pituitary Adenomas in Cushing's Disease

University Hospital, Basel, Switzerland — NA

TrialENROLLING BY INVITATION
Jan 2025Fimepinostat, Combination HDAC and Pi3-kinase Inhibitor Tumor-Directed Therapy for Cushing Disease

University of California, Los Angeles — PHASE2

TrialRECRUITING
Jun 2024Evaluation of Intraoperative Contrast Enhanced Ultrasound for the Identification of Pituitary Adenoma in Cushing's Disease Compared to Other Pituitary Tumors

Mayo Clinic

TrialRECRUITING
Nov 2023Evaluation of Positron Emission Tomography (PET) With [18F]FET for the Detection of ACTH-Secreting Corticotroph Pituitary Neuroendocrine Tumors.

Hospices Civils de Lyon

TrialRECRUITING
Dec 2020Postoperative Thrombosis Prevention in Patients With CD

Huashan Hospital — NA

TrialACTIVE NOT RECRUITING
Mar 2020

Isturisa: FDA approved

ISTURISA is a cortisol synthesis inhibitor indicated for the treatment of adult patients with Cushing®s disease for whom pituitary surgery is not an option or has not been curative.

FDAcompleted
Jul 2019Discriminant Capacity and Thresholds of Salivary Cortisol in Chemiluminescence in the Diagnosis of Hypercorticisms

Centre Hospitalier Universitaire de Nīmes

TrialACTIVE NOT RECRUITING
Mar 2019Long-Term Follow-Up of Survivors of Pediatric Cushing Disease

Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

3 programs

FINANCIAL LANDSCAPE SUMMARY

3

Total programs

3

Open now

2

Copay cards

Copay Assistance2

Signifor LAR

Recordati

OpenContact for detailsApply ↗

Signifor

Recordati

OpenContact for detailsApply ↗

Patient Assistance Programs1

Isturisa

Recordati Rare Diseases

OpenContact for detailsApply ↗

View all support programs on disease page →

Approved Treatments

2 FDA-approved

Isturisa

(osilodrostat)Orphan drug

Recordati Rare Diseases, Inc

12.1 Mechanism of Action Osilodrostat is a cortisol synthesis inhibitor. It inhibits 11beta-hydroxylase (CYP11B1), the enzyme responsible for the fina...

Approved Mar 2020FDA label ↗

Signifor

(pasireotide)Orphan drug

Novartis Pharmaceuticals Corporation

Somatostatin Analog [EPC]

12.1 Mechanism of Action SIGNIFOR is an injectable cyclohexapeptide somatostatin analogue. Pasireotide exerts its pharmacological activity via binding...

Approved Jun 2018FDA label ↗

View full treatment details on disease page →

Clinical Trial Landscape

9 active trials
2Phase 2
3N/A
4Unknown
9Total recruiting
Search clinical trials for Cushing disease

Recent News & Research

No recent news articles indexed yet for Cushing disease.
Search PubMed for Cushing disease

Browse all Cushing disease news →

Specialist Network

Top 6 by expertise

View all Cushing disease specialists →

Quick Actions