Congenital myopathy

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At a Glance

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Regulatory Watchboard

5 events
Nov 2025Smoking Cessation Intervention for Young Adults Using MTM: A Randomized Controlled Trial

University of Nevada, Las Vegas — NA

TrialNOT YET RECRUITING
Mar 2025Dose Response of Exercise for Arthritis Management

University of South Carolina — NA

TrialRECRUITING
Sep 2023Effectiveness of Ketogenic Diet in MELAS Syndrome

Second Affiliated Hospital, School of Medicine, Zhejiang University — NA

TrialNOT YET RECRUITING
Feb 2023Melpida: Recombinant Adeno-associated Virus (serotype 9) Encoding a Codon Optimized Human AP4M1 Transgene (hAP4M1opt)

Elpida Therapeutics SPC — PHASE1, PHASE2

TrialRECRUITING
Jul 2004Natural History Study - Mitochondrial Disease

Columbia University

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

0

Total programs

No financial assistance programs currently listed for Congenital myopathy.
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Clinical Trial Landscape

No active clinical trials currently recruiting for Congenital myopathy.
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Recent News & Research

No recent news articles indexed yet for Congenital myopathy.
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Specialist Network

Top 6 by expertise

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