Advocacy intelligence hub — real-time data for patient organizations
American Thrombosis and Hemostasis Network
PedNet Haemophilia Research Foundation
Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
FINANCIAL LANDSCAPE SUMMARY
Total programs
Ultragenyx Medical Director
Ultragenyx Pharmaceuticals Inc.
📍 Little Rock, Arkansas
Mirella Calcinai, MD
Medical Director, Clinical Development
Ri Liesner, Dr
Great Ormond Street Hospital
Ingrid Pabinger-Fasching, Prof.
Universitätsklinik für Innere Medizin I der Stadt Wien
Amy Shapiro, Dr
Co-Medical Director, Indiana Hemophilia and Thrombosis Center, 8402 Harcourt Road, Suite 420, Indianapolis, IN46260, USA
Tiffany Chang, MD
Spark Therapeutics, Inc.