Congenital dyserythropoietic anemia type I Advocacy Hub | UniteRare

At a Glance

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1FDA treatments

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1Specialists

Regulatory Watchboard

No FDA or trial events recorded yet for Congenital dyserythropoietic anemia type I.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

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No financial assistance programs currently listed for Congenital dyserythropoietic anemia type I.
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Approved Treatments

1 FDA-approved

Dyural 80-Lm

(METHYLPREDNISOLONE ACETATE, LIDOCAINE HYDROCHLORIDE, BUPIVACAINE HYDROCHLORIDE, POVIDINE IODINE, ISOPROPYL ALCOHOL)Orphan drugstandard

Advanced Rx Pharmacy of Tennessee, LLC

12.1 Mechanism of Action Bupivacaine blocks the generation and the conduction of nerve impulses, presumably by increasing the threshold for electrical...

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Clinical Trial Landscape

No active clinical trials currently recruiting for Congenital dyserythropoietic anemia type I.
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Recent News & Research

No recent news articles indexed yet for Congenital dyserythropoietic anemia type I.
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Specialist Network

Top 1 by expertise

Hisham Abdel-Azim, MD, MD

Childrens Hospital Los Angeles, University of Southern California

📍 LOS ANGELES, CA

Score 31 trial

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