Congenital adrenal hyperplasia

Advocacy intelligence hub — real-time data for patient organizations

View full disease page →Search clinical trials →
Download CSV

At a Glance

Live from database

Regulatory Watchboard

10 events
Jan 2026A Study in Pediatric Participants With Congenital Adrenal Hyperplasia (Balance-CAH)

Crinetics Pharmaceuticals Inc. — PHASE2, PHASE3

TrialRECRUITING
Dec 2025A Study to Evaluate Atumelnant in Adults With Congenital Adrenal Hyperplasia

Crinetics Pharmaceuticals Inc. — PHASE3

TrialRECRUITING
Sep 2025Pharmacokinetics, Safety and Tolerability of Crinecerfont in Participants With Congenital Adrenal Hyperplasia Who Are Less Than 2 Years Old

Neurocrine Biosciences — PHASE2

TrialRECRUITING
Apr 2025Syndromes With Neonatal Salt Loss: Not Only Congenital Adrenal Hyperplasia Due to 21-hydroxylase Deficiency (21OH-ISC)

IRCCS Azienda Ospedaliero-Universitaria di Bologna — NA

TrialRECRUITING
Feb 2025An Extension Study to Evaluate Safety and Efficacy in Participants Treated With CRN04894

Crinetics Pharmaceuticals Inc. — PHASE2

TrialRECRUITING
Dec 2024

Crenessity: FDA approved

adjunctive treatment to glucocorticoid replacement to control androgens in adults and pediatric patients 4 years of age and older with classic congenital adrenal hyperplasia (CAH)

FDAcompleted
Nov 2024Fertility And Sexual Function In CAH: CALLIOPE

University of Roma La Sapienza — NA

TrialRECRUITING
Dec 2022A Trial of Lu AG13909 in Participants With Congenital Adrenal Hyperplasia

H. Lundbeck A/S — PHASE1, PHASE2

TrialRECRUITING
Jun 2022Electronic Registry of Male Patients With Congenital Adrenal Hyperplasia 21-hydroxylase Deficiency

IRCCS Azienda Ospedaliero-Universitaria di Bologna

TrialRECRUITING
Jul 2021A Study of Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH)

Adrenas Therapeutics Inc — PHASE1, PHASE2

TrialACTIVE NOT RECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

1 program

FINANCIAL LANDSCAPE SUMMARY

1

Total programs

1

Open now

1

Copay cards

Copay Assistance1

Crenessity

Unknown

OpenContact for detailsApply ↗

View all support programs on disease page →

Approved Treatments

2 FDA-approved

Crenessity

(crinecerfont)Orphan drug

Neurocrine Biosciences, Inc.

Corticotropin-releasing Factor Type 1 Receptor Antagonist [EPC]

12.1 Mechanism of Action Crinecerfont is a selective corticotropin-releasing factor (CRF) type 1 receptor antagonist. Crinecerfont blocks the binding ...

Approved Dec 2024FDA label ↗

Dyural 80-Lm

(METHYLPREDNISOLONE ACETATE, LIDOCAINE HYDROCHLORIDE, BUPIVACAINE HYDROCHLORIDE, POVIDINE IODINE, ISOPROPYL ALCOHOL)Orphan drugstandard

Advanced Rx Pharmacy of Tennessee, LLC

12.1 Mechanism of Action Bupivacaine blocks the generation and the conduction of nerve impulses, presumably by increasing the threshold for electrical...

FDA label ↗

View full treatment details on disease page →

Clinical Trial Landscape

13 active trials
3Phase 3
1Phase 4
2Phase 2
2N/A
2Unknown
1PHASE2, PHASE3
2PHASE1, PHASE2
13Total recruiting
Search clinical trials for Congenital adrenal hyperplasia

Recent News & Research

No recent news articles indexed yet for Congenital adrenal hyperplasia.
Search PubMed for Congenital adrenal hyperplasia

Browse all Congenital adrenal hyperplasia news →

Specialist Network

Top 6 by expertise

View all Congenital adrenal hyperplasia specialists →

Quick Actions