Advocacy intelligence hub — real-time data for patient organizations
BioMarin Pharmaceutical — PHASE4
Agios Pharmaceuticals, Inc. — PHASE1
Peking University — NA
Peking University — NA
BioMarin Pharmaceutical — PHASE4
Rigshospitalet, Denmark — NA
University of Guelph — NA
University Medical Centre Ljubljana — NA
Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
FINANCIAL LANDSCAPE SUMMARY
Total programs
Debra Lounsbury
BioMarin Pharmaceutical
Rajavel Elango, Ph.D
University of British Columbia
Joshua Lilienstein, M.D., MD
BioMarin Pharmaceutical
📍 JAMAICA PLAIN, MA
Rajavel Elango, PhD
BC Children's Hospital Research Institute, University of British Columbia
📍 Vancouver, British Columbia
Anita MacDonald
Birmingham Women's and Children's NHS Foundation Trust
📍 Birmingham
Suyash Prasad, MD
BioMarin Pharmaceutical