Chronic myeloid leukemia

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At a Glance

Live from database

Regulatory Watchboard

10 events
May 2026Study to Determine the Efficacy and Safety of Asciminib in Pediatric Patients With Ph+ CML-CP

Novartis Pharmaceuticals — PHASE2

TrialNOT YET RECRUITING
May 2026Impact of Tyrosine Kinase Inhibitors on Glucose Level and Lipid Metabolism in Chronic Myeloid Leukemia Patients

Assiut University

TrialNOT YET RECRUITING
May 2026Phase II Study Assessing the Safety and Efficacy of Dasatinib in Combination With Ropeginterferon in Patients With Newly Diagnosed Chronic Myeloid Leukemia in Chronic Phase

M.D. Anderson Cancer Center — PHASE2

TrialNOT YET RECRUITING
Apr 2026DANZITEN: New indication approved
FDAcompleted
Mar 2026BOSULIF: New indication approved
FDAcompleted
Mar 2026BOSULIF: New indication approved
FDAcompleted
Feb 2026Real-world Study of Scemblix in the Treatment of Chronic Myeloid Leukemia in China

Novartis Pharmaceuticals

TrialNOT YET RECRUITING
Jan 2026Pacritinib vs. Hydroxyurea in Advanced Proliferative Chronic Myelomonocytic Leukemia

Theradex — PHASE2

TrialRECRUITING
Dec 2025Observational Study on Dose Optimization of Olverembatinib in Patients With Chronic Myeloid Leukemia in Chronic or Accelerated Phase

Qian Jiang

TrialENROLLING BY INVITATION
Nov 2025A Real-world Chronic Myelogenous Leukemia (CML) Patient Disease Registry to Describe Patient Experience and Clinical Outcomes Among Patients With CML Receiving Approved First or Second Line Tyrosine Kinase Inhibitor (TKI) Therapy

Novartis Pharmaceuticals

TrialNOT YET RECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

8 programs

FINANCIAL LANDSCAPE SUMMARY

8

Total programs

8

Open now

8

Copay cards

Copay Assistance8

Busulfan

Otsuka Pharmaceutical

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BOSULIF

Pfizer

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Synribo

IVAX International GmbH

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Nilotinib

Novartis

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SCEMBLIX

Novartis

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Roferon A

Hoffmann-La Roche, Inc.

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DANZITEN

Azurity

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Iclusig

Takeda

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Approved Treatments

7 FDA-approved

Danziten

(nilotinib)Orphan drug

Azurity Pharmaceuticals, Inc.

Kinase Inhibitor [EPC]

12.1 Mechanism of Action Nilotinib is an inhibitor of the BCR-ABL kinase. Nilotinib binds to and stabilizes the inactive conformation of the kinase do...

Approved Nov 2024FDA label ↗

Bosulif

(bosutinib)Orphan drug

PF PRISM C.V.

12.1 Mechanism of Action Bosutinib is a TKI. Bosutinib inhibits the BCR-ABL kinase that promotes CML; it is also an inhibitor of Src-family kinases in...

Approved Sep 2023FDA label ↗

Scemblix

(asciminib)Orphan drug

Novartis Pharmaceuticals Corporation

12.1 Mechanism of Action Asciminib is an ABL/BCR-ABL1 tyrosine kinase inhibitor. Asciminib inhibits the ABL1 kinase activity of the BCR::ABL1 fusion p...

Approved Oct 2021FDA label ↗

Synribo

(omacetaxine mepesuccinate)Orphan drug

IVAX International GmbH

Approved Oct 2012

Roferon A

(Interferon alfa-2a)Orphan drug

Hoffmann-La Roche, Inc.

Approved Oct 1995

Busulfex

(Busulfan)Orphan drugstandard

Otsuka Pharmaceutical Company, Ltd

Alkylating Drug [EPC]

12.1 Mechanism of Action Busulfan is a bifunctional alkylating agent in which two labile methanesulfonate groups are attached to opposite ends of a fo...

FDA label ↗

Iclusig

(ponatinib)Orphan drugstandard

Takeda Pharmaceuticals U.S.A., Inc.

12.1 Mechanism of Action Ponatinib is a kinase inhibitor. Ponatinib inhibited the in vitro tyrosine kinase activity of ABL and T315I mutant ABL with I...

FDA label ↗

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Clinical Trial Landscape

29 active trials
4Phase 3
1Phase 4
8Phase 2
2Phase 1
1N/A
11Unknown
2PHASE1, PHASE2
29Total recruiting
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Recent News & Research

6 articles
Future medicinal chemistryApr 21, 2026

Importance of five membered heterocyclic compounds in treatment of chronic myeloid leukemia by targeting various pathways.

Chronic myeloid leukemia (CML) is a clonal hematopoietic malignancy characterized by the presence of the Philadelphia chromosome, which generates the constitutively active BCR::ABL1 tyrosine kinase, d...

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Journal of physiology and biochemistryApr 20, 2026

Roles of extracellular vesicles in the pathogenesis of chronic myeloid leukemia.

Extracellular vesicles (EVs) are lipid bilayer-enclosed particles released by cells into the extracellular space. They are produced by the majority of cell types under both physiological and pathologi...

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International journal of hematologyApr 15, 2026

Development of a blood test-based predictive scoring tool for treatment response in chronic myeloid leukemia.

The European LeukemiaNet recommendations for the management of chronic myeloid leukemia (CML) consider achievement of major molecular response (MMR) within 12 months to be an optimal response (OR...

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BiologyApr 13, 2026

An AI-Enabled Single-Cell Transcriptomic Analysis Pipeline for Gene Signature Discovery in Natural Killer Cells Linked to Remission Outcomes in Chronic Myeloid Leukemia.

A major technical challenge in single-cell transcriptomics is the absence of an integrative analytic pipeline that can simultaneously leverage gene regulatory network (GRN) architecture, AI-assisted g...

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Expert review of hematologyApr 6, 2026

Evolution of the European LeukemiaNet recommendations for chronic myeloid leukemia.

Chronic myeloid leukemia (CML) management has been revolutionized by tyrosine kinase inhibitors (TKIs), leading to near-normal life expectancy for most patients diagnosed in the chronic phase. The Eur...

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CancersMar 28, 2026

Targeting Mitochondrial Vulnerabilities in Chronic Myeloid Leukemia: From Pathobiology to Novel Therapeutic Opportunities.

Background : Mitochondria are multifunctional organelles that play a central role in maintaining cellular homeostasis by regulating energy metabolism, reactive oxygen species (ROS) generation, ion hom...

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