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FINANCIAL LANDSCAPE SUMMARY
Total programs
Strensiq
(ASFOTASE ALFA)Orphan drugstandardAlexion Pharmaceuticals, Inc.
Tissue-nonspecific Alkaline Phosphatase [EPC]
12.1 Mechanism of Action HPP is caused by a deficiency in TNSALP enzyme activity, which leads to elevations in several TNSALP substrates, including in...