Charcot-Marie-Tooth disease type 4J Advocacy Hub | UniteRare

At a Glance

Live from database

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1Recruiting trials

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2Specialists

Regulatory Watchboard

2 events

Apr 2026Study of Intrathecal ELP-02 for Charcot-Marie-Tooth Disease Type 4J (CMT4J)

Elpida Therapeutics SPC — PHASE1, PHASE2

TrialNOT YET RECRUITING

Jul 2024A Prospective Natural History and Outcome Measure Discovery Study of Charcot-Marie-Tooth Disease, Type 4J

Elpida Therapeutics SPC

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

Total programs

No financial assistance programs currently listed for Charcot-Marie-Tooth disease type 4J.
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Clinical Trial Landscape

1 active trial

1Unknown

1Total recruiting

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Recent News & Research

No recent news articles indexed yet for Charcot-Marie-Tooth disease type 4J.
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Specialist Network

Top 2 by expertise

Davide Pareyson, MD

Fondazione IRCCS Istituto Neurologico Carlo Besta

Score 281 trial

Souad Messahel, Ph.D

Elpida Therapeutics SPC

Score 31 trial

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