Cerebrotendinous xanthomatosis

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At a Glance

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Regulatory Watchboard

10 events
Mar 2026Dual-Target Nectin-4/HER2 CAR-NK Cells in Advanced Urothelial Carcinoma

Beijing Biotech — PHASE1

TrialRECRUITING
Nov 2025A Study to Evaluate LY3537021 for the Treatment of Nausea and Vomiting Caused by Chemotherapy in Adults With Cancer

Eli Lilly and Company — PHASE2

TrialRECRUITING
Nov 2025Toripalimab Combined With Anthracycline-free or Anthracycline-containing Chemotherapy as Neoadjuvant Chemotherapy for Early Triple Negative Breast Cancer

Henan Cancer Hospital — PHASE2

TrialNOT YET RECRUITING
Sep 2025A Phase I/II Study of TRS005 in Combination With Cyclophosphamide, Doxorubicin, and Prednisone(T-CHP) in Previously Untreated Patients With CD20-positive DLBCL

Zhejiang Teruisi Pharmaceutical Inc. — PHASE1, PHASE2

TrialNOT YET RECRUITING
Aug 2025A Phase Ib Study of Novel Combination (New) of Low Dose Oral CyclophoSphamide (s) to Potentiate Axatilimab (A) + Retifanlimab (R) in Treating Metastatic Triple Negative Breast Cancer (TNBC)

M.D. Anderson Cancer Center — PHASE1

TrialRECRUITING
Aug 2025Testing the Investigational Agent Combination of Daratumumab, Bortezomib, and Dexamethasone Compared to the Usual Treatment of Cyclophosphamide, Bortezomib, and Dexamethasone in Newly Diagnosed Multiple Myeloma Patients With Kidney Failure

Eastern Cooperative Oncology Group — PHASE2

TrialNOT YET RECRUITING
Jul 2025Early Use of Tacrolimus in HLA-Mismatched Haploidentical Allogeneic Hematopoietic Transplantation With Post-Transplant Cyclophosphamide

Northside Hospital, Inc. — PHASE2

TrialRECRUITING
May 2025Comparing Neoadjuvant/Adjuvant GVAX vs a mKRASvax Given With Anti-PD-1 and Anti-CD137 for Surgically Resectable Pancreatic Cancer

Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins — PHASE1, PHASE2

TrialRECRUITING
May 2025Tirzepatide vs Liraglutide in Bone

National and Kapodistrian University of Athens

TrialRECRUITING
Mar 2025Atezolizumab and Chemotherapy Treatment as T-cell Activators in Metastatic Triple Negative Breast Cancer Patients

European Institute of Oncology — PHASE2

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

1 program

FINANCIAL LANDSCAPE SUMMARY

1

Total programs

1

Open now

Patient Assistance Programs1

Chenix

Solvay

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Approved Treatments

1 FDA-approved

Chenix

(chenodiol)Orphan drugstandard

Solvay

Bile Acid [EPC]

12.1 Mechanism of Action Endogenous chenodiol (chenodeoxycholic acid) is a primary bile acid, synthesized from cholesterol in the liver. In CTX, the m...

FDA label ↗

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Clinical Trial Landscape

No active clinical trials currently recruiting for Cerebrotendinous xanthomatosis.
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Recent News & Research

No recent news articles indexed yet for Cerebrotendinous xanthomatosis.
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Specialist Network

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