Canavan disease

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At a Glance

Live from database

Regulatory Watchboard

3 events
Sep 2021A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)

Aspa Therapeutics — PHASE1, PHASE2

TrialRECRUITING
Apr 2021rAAV-Olig001-ASPA Gene Therapy for Treatment of Children With Typical Canavan Disease

Myrtelle Inc. — PHASE1, PHASE2

TrialENROLLING BY INVITATION
Oct 2019Natural History Study of Patients With Canavan Disease (CANinform Study)

Aspa Therapeutics — NA

TrialACTIVE NOT RECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

0

Total programs

No financial assistance programs currently listed for Canavan disease.
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Clinical Trial Landscape

3 active trials
1N/A
2PHASE1, PHASE2
3Total recruiting
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Recent News & Research

No recent news articles indexed yet for Canavan disease.
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Specialist Network

Top 6 by expertise

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