Beta-thalassemia

Advocacy intelligence hub — real-time data for patient organizations

View full disease page →Search clinical trials →
Download CSV

At a Glance

Live from database

Regulatory Watchboard

10 events
Jan 2027Heterologous Cord Blood-Derived Red Blood Cell for Transfusion in Extremely Preterm Infants

Hospital Clinic of Barcelona — NA

TrialNOT YET RECRUITING
Jul 2026Association of Micro RNA-155 With Alloimmunization in Transfusion-Dependent Patients

Assiut University

TrialNOT YET RECRUITING
Feb 2026A Real-World Study to Evaluate Luspatercept in Adults With Transfusion-Dependent Beta-Thalassemia in the Middle East

Bristol-Myers Squibb

TrialRECRUITING
Dec 2025

AQVESME: FDA approved

treatment of anemia in adults with alpha- or beta-thalassemia

FDAcompleted
Dec 2025Gonadal Function in Thalassemic Patient

Sohag University

TrialNOT YET RECRUITING
Nov 2025Use of the Hemanext One® Hypoxic Red Blood Cell Storage System for Transfusion in Thalassemia Patients

University Research Institute for the Study of Genetic & Malignant Disorders in Childhood

TrialENROLLING BY INVITATION
Oct 2025Body Composition in Pediatric Patients With Thalassemia Major

Assiut University

TrialNOT YET RECRUITING
Sep 2025Evaluation of Physiological and Psychological Factors Involved in Exercise Intolerance in Patients With β-TTD

Centre Hospitalier Metropole Savoie — NA

TrialRECRUITING
Aug 2025Evaluating the Effect of N-Acetyl Cysteine and Alpha Lipoic Acid in Patients With Beta Thalassemia

Tanta University — PHASE3

TrialNOT YET RECRUITING
Aug 2025A Clinical Study of Ultra-transplantation for the Treatment of Major Thalassemia Scheme

Hu Peng — NA

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

2 programs

FINANCIAL LANDSCAPE SUMMARY

2

Total programs

2

Open now

1

Copay cards

Copay Assistance1

Reblozyl

Bristol Myers Squibb

OpenContact for detailsApply ↗

Patient Assistance Programs1

AQVESME

Agios Pharmaceuticals, Inc.

OpenContact for detailsApply ↗

View all support programs on disease page →

Approved Treatments

2 FDA-approved

AQVESME

(MITAPIVAT)Orphan drug

Agios Pharmaceuticals, Inc.

Approved Dec 2025FDA label ↗

Reblozyl

(LUSPATERCEPT)Orphan drugstandard

Celgene Corporation

FDA label ↗

View full treatment details on disease page →

Clinical Trial Landscape

44 active trials
2Phase 3
2Phase 4
8Phase 2
2Phase 1
9N/A
11Unknown
6PHASE1, PHASE2
4EARLY_PHASE1
44Total recruiting
Search clinical trials for Beta-thalassemia

Recent News & Research

No recent news articles indexed yet for Beta-thalassemia.
Search PubMed for Beta-thalassemia

Browse all Beta-thalassemia news →

Specialist Network

Top 6 by expertise

View all Beta-thalassemia specialists →

Quick Actions