Autosomal recessive malignant osteopetrosis

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At a Glance

Live from database

Regulatory Watchboard

1 event
Feb 2000

Actimmune: FDA approved

Delaying time to disease progression in patients with severe, malignant osteopetrosis.

FDAcompleted

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

1 program

FINANCIAL LANDSCAPE SUMMARY

1

Total programs

1

Open now

Patient Assistance Programs1

Actimmune

Horizon Therapeutic Ireland DAC

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Approved Treatments

1 FDA-approved

Actimmune

(Interferon gamma 1-b)Orphan drug

Horizon Therapeutic Ireland DAC

Interferon gamma [EPC]

12.1 Mechanism of Action Interferons bind to specific cell surface receptors and initiate a sequence of intracellular events that lead to the transcri...

Approved Feb 2000FDA label ↗

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Clinical Trial Landscape

No active clinical trials currently recruiting for Autosomal recessive malignant osteopetrosis.
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Recent News & Research

No recent news articles indexed yet for Autosomal recessive malignant osteopetrosis.
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Specialist Network

Top 2 by expertise

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