Autosomal recessive hypophosphatemic rickets Advocacy Hub | UniteRare

At a Glance

Live from database

🔬

3Recruiting trials

🩺

4Specialists

Regulatory Watchboard

4 events

Mar 2025ENERGY 2: Evaluation of the Efficacy and Safety of INZ-701 in Infants With ENPP1 Deficiency

Inozyme Pharma — PHASE3

TrialRECRUITING

Jul 2024PROPEL - A Prospective Observational Patient Registry to Evaluate ENPP1 and ABCC6 Deficiency

Inozyme Pharma

TrialRECRUITING

Nov 2023The ENERGY 3 Study: Evaluation of Efficacy and Safety of INZ-701 in Children With ENPP1 Deficiency

Inozyme Pharma — PHASE3

TrialACTIVE NOT RECRUITING

Jun 2023The ENERGY Study: Evaluation of Safety and Tolerability of INZ-701 in Infants With ENPP1 Deficiency or ABCC6 Deficiency

Inozyme Pharma — PHASE1

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

Total programs

No financial assistance programs currently listed for Autosomal recessive hypophosphatemic rickets.
Check the disease page for updates →

Clinical Trial Landscape

3 active trials

2Phase 3

1Phase 1

3Total recruiting

Search clinical trials for Autosomal recessive hypophosphatemic rickets →

Recent News & Research

No recent news articles indexed yet for Autosomal recessive hypophosphatemic rickets.
Search PubMed for Autosomal recessive hypophosphatemic rickets →

Browse all Autosomal recessive hypophosphatemic rickets news →

Specialist Network

Top 4 by expertise

Kurt Gunter, MD, M.D

Inozyme Pharma, Inc.

📍 BEVERLY, MA

Score 288 trials

Pedro Huertas, MD, M.D

Inozyme Pharma

📍 CONCORD, MA

Score 61 trial

Carlos R Ferreira Lopez, M.D.

Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)

📍 Bethesda, Maryland

Score 42 trials

Alex Lai, MD

Inozyme Pharma

Score 41 trial1 pub

View all Autosomal recessive hypophosphatemic rickets specialists →

Quick Actions

📄

View Disease Page

Full profile, treatments, community

🔬

Search Clinical Trials

Find recruiting studies now

🩺

Find Specialists

Ranked by expertise & trials

💰

Financial Assistance

Copay cards, PAPs, grants

📰