Autosomal dominant Charcot-Marie-Tooth disease type 2D

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At a Glance

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Regulatory Watchboard

1 event
Oct 2025Personalized Antisense Oligonucleotide for A Single Participant With GARS1 Gene Mutation Associated With Charcot-Marie-Tooth Disease Type 2D (CMT2D)

n-Lorem Foundation — PHASE1, PHASE2

TrialENROLLING BY INVITATION

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

0

Total programs

No financial assistance programs currently listed for Autosomal dominant Charcot-Marie-Tooth disease type 2D.
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Clinical Trial Landscape

1 active trial
1PHASE1, PHASE2
1Total recruiting
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Recent News & Research

No recent news articles indexed yet for Autosomal dominant Charcot-Marie-Tooth disease type 2D.
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Specialist Network

No specialists currently listed for Autosomal dominant Charcot-Marie-Tooth disease type 2D.

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