Advocacy intelligence hub — real-time data for patient organizations
Assistance Publique - Hôpitaux de Paris — NA
Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
FINANCIAL LANDSCAPE SUMMARY
Total programs
Loargys
(pegzilarginase-nbln)Orphan drugImmedica Pharma AB
12.1 Mechanism of Action ARG1-D is an inherited metabolic disease characterized by deficiency of the arginase 1 enzyme and associated with the persist...
Valérie Li Thiao Te
Service d'Oncologie-Hématologie Pédiatrique
Maïlys Le Guyader
Service d'Hématologie Biologique
Annelise Voyer
Service d'Hématologie Biologique
Charlotte Durand-Maugard
Laboratoire de Biochimie
Antoine Galmiche
Laboratoire de Biochimie
Tasnim Bel Hadj
Service d'Hématologie Biologique