Advocacy intelligence hub — real-time data for patient organizations
Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
FINANCIAL LANDSCAPE SUMMARY
Total programs
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Patient Assistance Programs1
Harliku
Cycle Pharmaceuticals Ltd.
Harliku
(nitisinone)Orphan drugCycle Pharmaceuticals Ltd.
4-Hydroxyphenyl-Pyruvate Dioxygenase Inhibitor [EPC]
12.1 Mechanism of Action Nitisinone is a competitive inhibitor of hydroxyphenyl-pyruvate dioxygenase, an enzyme upstream of homogentisate 1,2-dioxygen...
L Ranganath
Royal Liverpool & Broadgreen University Hospitals NHS Truts
Jean-Baptiste Arnoux
Hopital Necker-Enfants Malades
Wendy J Introne, M.D.
National Human Genome Research Institute (NHGRI)
📍 Bethesda, Maryland
Anita MacDonald
Birmingham Women's and Children's NHS Foundation Trust
📍 Birmingham
William L Nyhan, MD, PhD
University of California, San Diego
Birgitta Olsson
Garriguella AB