Advocacy intelligence hub — real-time data for patient organizations
Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
FINANCIAL LANDSCAPE SUMMARY
Total programs
Priya Kishnani, MD
Duke University
📍 DURHAM, NC
Raphael Schiffmann, M.D, M.H.Sc
Institute of Metabolic Disease
Deberah S Goldman, Ph.D
Adult Polyglucosan Body Disease Research Foundation
📍 GREAT NECK, NY
Deeksha S Bali
Duke University Medical Center
Peter B Kang
University of Minnesota Medical School
Ariana L Smith
University of Pennsylvania Health System