Adult-onset distal myopathy due to VCP mutation Advocacy Hub | UniteRare

At a Glance

Live from database

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2FDA treatments

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2Open funds

Regulatory Watchboard

No FDA or trial events recorded yet for Adult-onset distal myopathy due to VCP mutation.

Financial Assistance

2 programs

FINANCIAL LANDSCAPE SUMMARY

Total programs

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Patient Assistance Programs2

TAFINLAR

Novartis Pharmaceuticals Corp.

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MEKINIST and TAFINLAR

Novartis Pharmaceuticals Corporation

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Approved Treatments

2 FDA-approved

MEKINIST and TAFINLAR

(trametinib and dabrafenib)Orphan drugaccelerated

Novartis Pharmaceuticals Corporation

MEKINIST

(trametinib)Orphan drugstandard

Novartis Pharmaceuticals Corp.

12.1 Mechanism of Action Trametinib is a reversible inhibitor of mitogen-activated extracellular signal-regulated kinase 1 (MEK1) and MEK2 activation ...

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Clinical Trial Landscape

No active clinical trials currently recruiting for Adult-onset distal myopathy due to VCP mutation.
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Recent News & Research

No recent news articles indexed yet for Adult-onset distal myopathy due to VCP mutation.
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Specialist Network

No specialists currently listed for Adult-onset distal myopathy due to VCP mutation.

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