3-hydroxyacyl-CoA dehydrogenase deficiency

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At a Glance

Live from database

Regulatory Watchboard

2 events
Feb 2023A Study to Determine the Effect of Triheptanoin Compared With Even-Chain MCT on MCEs in Pediatric Patients With LC-FAOD

Ultragenyx Pharmaceutical Inc — PHASE3

TrialACTIVE NOT RECRUITING
Nov 2021Long-Chain Fatty Acid Oxidation Disorders In-Clinic Disease Monitoring Program

Ultragenyx Pharmaceutical Inc

TrialACTIVE NOT RECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

0

Total programs

No financial assistance programs currently listed for 3-hydroxyacyl-CoA dehydrogenase deficiency.
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Clinical Trial Landscape

2 active trials
1Phase 3
1Unknown
2Total recruiting
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Recent News & Research

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Specialist Network

Top 6 by expertise

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