2-hydroxyglutaric aciduria

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At a Glance

Live from database

Regulatory Watchboard

1 event
Jul 2025An Individual Patient, Open Label Study to Use ACER-001 to Treat Combined D,L-2 Hydroxyglutaric Aciduria (C-2HGA)

Jerry Vockley, MD, PhD — PHASE1

TrialENROLLING BY INVITATION

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

0

Total programs

No financial assistance programs currently listed for 2-hydroxyglutaric aciduria.
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Clinical Trial Landscape

1 active trial
1Phase 1
1Total recruiting
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Recent News & Research

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Specialist Network

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